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Rare Diseases

New treatment for advanced epithelioid sarcoma

The U.S. Food and Drug Administration (FDA) recently approved Epizyme, Inc’s tazemetostat (TAZVERIK) for the treatment of adult and pediatric patients with metastatic or advanced epithelioid sarcoma (AES). AES is a rare sarcoma that affects...

FDA to host meeting on the development of products for rare diseases

On February 24, the U.S. Food and Drug Administration (FDA) is hosting a public meeting to celebrate FDA Rare Disease Day 2020 which will focus on what the future holds for the product development...

Understanding & identifying rare liver disorder

In recognition of National Liver Awareness Month, American Nurse Today highlights a condition often overlooked and misunderstood, leading to misdiagnosis or underdiagnosis: Hepatic encephalopathy (HE). HE is a chronic liver condition that manifests itself in...